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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Dystrophie Musculaire de Becker BMD
Skeletal muscle
Muscle development
Muscles/physiopathology
Energy Metabolism/drug effects
DMO
NAD+
Activin Receptors
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
CaVβs
Muscle Strength
Gene modifiers
L-Type
Mdx mouse
Knockout
Dystrophy
Diseases
Morphogenesis
Muscular Atrophy
Cell homeostasis
Mice
Drp1
Long QT
LncRNA
Male
Multi exon skipping
Dystrophin
Animals
Cachexia
Gene expression
CD38
Cardiomyopathie
Inhibitors
Dynamin 2
LKB1
Liver
Immunoglobulin Fc Fragments/pharmacology
MiARN
Cells
Inbred C57BL
Humans
BMD
Dystrophin central domain
Clinical trials
Multi resolution modeling
Duchenne muscular dystrophy DMD
Myogenesis
Multiresolution modeling
Muscle
Becker muscular dystrophy
Muscular Dystrophy
Antisense oligonucleotides
Cell Line
Becker BMD muscular dystrophy
Human Umbilical Vein Endothelial Cells
Hear
Dystrophin-EGFP
Muscle Biology
Gene Expression Regulation/drug effects
LncARN
Duchenne DMD dystrophy
Dystrophie musculaire de Becker
Animal/physiopathology
Duchenne muscular dystrophy
Cell Biology
Allele‐specific silencing therapy
Dystrophine
MES
DMD
Génomique
Calcium
Mitochondrial fission
Muscular dystrophy
CTNNB1
Invivo
Autophagy
Base Sequence
Epigenetics
Myotendinous junction
Long noncoding RNA
Molecular docking
Centronuclear myopathy
Ex-vivo
Calcium Channels
Becker muscular dystrophy BMD
Homeostasis
CaV subunits
Delivery
Dystrophie Musculaire de Duchenne DMD
NNOS
Cultured
Inbred mdx
Hepatocellular carcinoma
Modificateurs de gènes
DHPR α1S
Exon skipping
Molecular Sequence Data
Genomic
Cardiomyopathy
Metabolism